In a study published in Nature Communications, scientists reported a novel strategy to deliver the CRISPR-Cas9 gene-editing system into the lungs of a cystic fibrosis mouse ... was sufficient to ...

Cystic fibrosis is a genetic disorder that causes a problem in the channel in your body called the chloride channel and what that does is that it makes it that you get thick secretions in your ...

They do not have enough abnormal chloride channels to cause the labored breathing and clogged pancreas of cystic fibrosis, but they do have enough of a defect to prevent the cholera from taking hold.

In November 1998, Martin Burke was on his first clinical rotation in the MD/PhD program at Harvard Medical School when he met a 22-year-old cystic fibrosis patient who was taking 17 different ...

An inhaled gene therapy for cystic fibrosis developed by Boehringer Ingelheim ... a disease caused by an imbalance in chloride and sodium ions in the body that results in thick, sticky mucus ...

A new study supports the clinical utility of human nasal epithelial cultures as predictive biomarkers for cystic fibrosis CFTR modulator therapy.

Cystic fibrosis(CF) diagnosis has evolved with new consensus guidelines emphasizing the importance of genetic testing and sweat chloride measurements for accurate detection. According to the ...

Vertex Pharmaceuticals (Nasdaq: VRTX) today announced that the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for ALYFTREK ® ...

Advanced cystic ... cystic fibrosis, which causes thick, sticky mucus to build up in the body. It occurs when the so-called CFTR protein is not made or not made correctly, allowing chloride ...