In a study published in Nature Communications, scientists reported a novel strategy to deliver the CRISPR-Cas9 gene-editing system into the lungs of a cystic fibrosis mouse ... was sufficient to ...

In November 1998, Martin Burke was on his first clinical rotation in the MD/PhD program at Harvard Medical School when he met a 22-year-old cystic fibrosis patient who was taking 17 different ...

A new study supports the clinical utility of human nasal epithelial cultures as predictive biomarkers for cystic fibrosis CFTR modulator therapy.

Cystic fibrosis(CF) diagnosis has evolved with new consensus guidelines emphasizing the importance of genetic testing and sweat chloride measurements for accurate detection. According to the ...

Vertex Pharmaceuticals (Nasdaq: VRTX) today announced that the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for ALYFTREK ® ...

“Our goal has always been to serially innovate to help people with cystic fibrosis live healthier ... gets them closer to normal levels of sweat chloride,” said Carmen Bozic, M.D., Executive ...