For decades, a genetic test that turned up a mutation linked to inherited blindness was treated as a verdict, not a risk ...

The company has started enrolling patients into a run-in period for the Phase III study, and plans to begin dosing later this ...

Genetic variants believed to cause blindness in nearly everyone who carries them actually lead to vision loss less than 30% ...

Study supports favorable safety and tolerability profile and clinically meaningful functional and structural benefits in Stargardt disease ...

Researchers at University College Dublin (UCD) have discovered that a mutation in a gene called emc1 causes major vision ...

Multi-asset pipeline with significant targeted data readouts and milestones -- Two lead ophthalmic gene therapy programs in clinical trials ...

Researchers from Radboud university medical center and University of Basel have discovered new genetic causes of inherited ...